Research at Boston Children's Hospital

The research enterprise at Boston Children’s Hospital, comprising more than 3,000 researchers, is the world’s largest at a pediatric center. Our work is fueled by a deep understanding of disease coupled with world-class discovery platforms, including genetics and genomics, gene editing, bioinformatics, proteomics, bioengineering, image analysis, multiple animal models, biobanks and disease-specific stem cell lines. We have special expertise in rare disease discovery and see large, highly diverse patient populations.

michael rogers and danielle peterse

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More than 3,000 researchers & scientific staff

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1 million square feet of research space — and growing

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$388 million in total research funding FY2018 — #1 NIH funding for pediatric research

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A new frontier: Inside a custom drug

Dr. Yu and his team of scientists pulled off something unprecedented, something seemingly impossible. In the space of 10 months, they pinpointed Mila’s rare mutation, designed a drug to bypass it, engaged industry partners and FDA regulators, and launched a treatment trial — just for Mila.

Early encouraging results are reported in The New England Journal of Medicine. They could open a new path, showing it’s possible to create personalized genetic therapies for children with rare conditions — and to do so quickly.

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Dr. Yu batten disease

Boston Children's Hospital Innovation

BCH Innovation News @BCH_Innovation 11/21/2019 8:51:07 PM
RT @ncats_nih_gov: To fight deadly and aggressive childhood brain tumors, researchers from NCATS, @StanfordMed and @DFBC_PedCare created a…
BCH Innovation News @BCH_Innovation 11/21/2019 8:00:01 PM
Face blindness in #stroke provides leads for understanding #faceprocessing in #tuberoussclerosis and #autism:
BCH Innovation News @BCH_Innovation 11/21/2019 4:30:00 PM
The use of fiberoptic confocal microscopy may decrease the risk of injury inside the #heart during #cardiacsurgery:
BCH Innovation News @BCH_Innovation 11/21/2019 2:00:01 PM
Cambridge startup, @CRISPRTX, and partner @VertexPharma reached a significant milestone this week, releasing promis…
BCH Innovation News @BCH_Innovation 11/20/2019 8:00:00 PM
Researchers at @MIT use new technique that identifies T cells that produce inflammation seen in patients with certa…
BCH Innovation News @BCH_Innovation 11/20/2019 6:00:01 PM
Pulse electric fields offer a new, noninvasive way to profile #cancer tissue: via @xpress_medical
Building on our extraordinary leadership in pediatric science at Boston Children’s, we translate our findings — and those of others — to fundamentally change how disease is treated and cured.

David A. Williams, MD
Senior Vice President and Chief Scientific Officer